Enzyme Replacement Therapy (ERT) on Heart Function Changes the Outcome in Patients with Infantile-Onset Pompe Disease: A Familial History

<div>(a) Cardiac hypertrophy in a 6 months patient (XX) with DGAA; (b) cardiac hypertrophy in an infant (XY) with DGAA; (c) regression of cardiac hypertrophy in patient (XY) after 15 months of ERT.</div>

Case Reports in Pediatrics

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Figure 1

Figure 1: Enzyme Replacement Therapy (ERT) on Heart Function Changes the Outcome in Patients with Infantile-Onset Pompe Disease: A Familial History 